Glycogen storage disease type II

Results: 169



#Item
131Hepatology / Duke University / Medical genetics / Medicine / Health / Glycogen storage disease type II

You are cordially invited to attend the 2nd Annual INFANTILE Pompe Patient Meeting Hosted by the

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Source URL: www.unitedpompe.com

Language: English - Date: 2014-06-10 17:43:15
132Glycogen storage disease type II / Hepatology / BioMarin Pharmaceutical / Sanofi / Alglucosidase alfa / Genzyme / Clinical trial / ClinicalTrials.gov / Medicine / Health / Science

BioMarin is currently seeking patients for a Phase 3 clinical trial in Late Onset Pompe Disease. This phase 3 study incorporates a switchover design in which all patients switch directly from Myozyme® or Lumizyme® 1to

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Source URL: www.unitedpompe.com

Language: English - Date: 2014-06-16 18:19:57
133Epidemiology / Lysosomal storage diseases / Glycogen storage disease type II / Hepatology / Extraordinary Measures / John Crowley / William Canfield / Adrenoleukodystrophy / Clinical trial / Health / Medicine / Rare diseases

Dolencias extraordinarias, medidas extremas

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Source URL: ec.europa.eu

Language: English - Date: 2013-09-27 09:59:11
134Lysosomal storage diseases / Prevention / Screening / Glycogen storage disease type II / Health / Medicine / Rare diseases

PDF Document

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Source URL: www.agsd.org.uk

Language: English - Date: 2014-04-14 15:27:49
135

非売品 糖 原 病 Ⅱ 型︵ ポ ン ペ 病 ︶診 断 治 療 ガ イ ド ラ イ ン Glycogen Storage Disease Type II I

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Source URL: www.pmdrinsho.jp

Language: Japanese - Date: 2008-03-18 20:26:40
    136Glycogen storage disease type II / Hepatology / Alglucosidase alfa / Infusion pump / Lorazepam / Medicine / Health / Organochlorides

    HIGHLIGHTS OF PRESCRIBING INFORMATION These highlights do not include all the information needed to use MYOZYME safely and effectively. See full prescribing information for MYOZYME. MYOZYME® (alglucosidase alfa) Injecta

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    Source URL: www.myozyme.com

    Language: English - Date: 2014-05-27 09:58:04
    137Pharmaceutical sciences / Genzyme / Sanofi / Orphan drugs / Glycogen storage disease type II / Alglucosidase alfa / Prescription Drug User Fee Act / Imiglucerase / Alpha-galactosidase / Medicine / Health / Food and Drug Administration

    United States Court of Appeals For the First Circuit No[removed]IN RE: GENZYME CORP. SECURITIES LITIGATION,

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    Source URL: www.courthousenews.com

    Language: English - Date: 2014-06-10 11:20:05
    138Lipid storage disorders / Neurodegenerative disorders / Drug discovery / Epidemiology / Orphan drug / Orphan Drug Act / Niemann–Pick disease / Rare Disease Day / Glycogen storage disease type II / Health / Medicine / Rare diseases

    Combating Rare Diseases in the 21st Century The Orphan Drug Act What is a Rare Disease?

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    Source URL: www.chi.org

    Language: English - Date: 2014-02-27 15:16:35
    139Alglucosidase alfa / Glycogen storage disease type II / Prescription Drug User Fee Act / FDA Fast Track Development Program / Genzyme / William Canfield / Medicine / Health / Food and Drug Administration

    We would like to take this opportunity to provide an important update to the Pompe Community

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    Source URL: www.unitedpompe.com

    Language: English - Date: 2008-11-19 13:27:56
    140Rare diseases / Lysosomal storage diseases / Inborn errors of carbohydrate metabolism / Muscular system / Glycogen storage disease type II / Hepatology / Cardiomegaly / Mitochondrial disease / Duchenne muscular dystrophy / Health / Anatomy / Medicine

    Microsoft PowerPoint - PompesRehab-Carter [Read-Only]

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    Source URL: www.unitedpompe.com

    Language: English - Date: 2007-09-13 18:17:02
    UPDATE